Reviewed by Peptide Treatments Medical Advisory Board (Medical Advisory Board)

Taltirelin: Evidence Summary

Evidence summary for Taltirelin across studied indications. Each indication is graded using our evidence tier system based on the quality and quantity of available clinical data.

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Indication Evidence Tier Trial Count Summary
Spinocerebellar ataxia Tier B 4 Multiple Japanese RCTs; PMDA approved (Ceredist); modest motor improvement
Cerebellar degeneration (other) Tier C 1 Limited data outside primary spinocerebellar indication

References (2)

  1. A placebo-controlled study of taltirelin in patients with spinocerebellar degeneration — Kanazawa I, et al. . Journal of Neurology (1997) PMID: 39428104
  2. Randomized, double-blind, placebo-controlled trial of taltirelin in spinocerebellar degeneration — Kinoshita M, et al. . Neurological Sciences (2024)