Reviewed by Peptide Treatments Medical Advisory Board (Medical Advisory Board)

PCSK9 Inhibitors: Evidence Summary

Evidence summary for PCSK9 Inhibitors across studied indications. Each indication is graded using our evidence tier system based on the quality and quantity of available clinical data.

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Indication Evidence Tier Trial Count Summary
LDL cholesterol reduction Tier A 50 Consistent 50-60% LDL-C reduction across 50+ RCTs
Cardiovascular event prevention Tier A 3 FOURIER and ODYSSEY OUTCOMES demonstrated 15% MACE reduction
Familial hypercholesterolemia Tier A 10 FDA-approved indication with robust evidence

References (4)

  1. Evolocumab and Clinical Outcomes in Patients with Cardiovascular Disease — Sabatine MS, Giugliano RP, Keech AC, et al. . New England Journal of Medicine (2017) PMID: 28304224
  2. Alirocumab and Cardiovascular Outcomes after Acute Coronary Syndrome — Schwartz GG, Steg PG, Szarek M, et al. . New England Journal of Medicine (2018) PMID: 30403574
  3. Two Phase 3 Trials of Inclisiran in Patients with Elevated LDL Cholesterol — Ray KK, Wright RS, Kallend D, et al. . New England Journal of Medicine (2020) PMID: 32187462
  4. Efficacy and Safety of Alirocumab in Reducing Lipids and Cardiovascular Events — Robinson JG, Farnier M, Krempf M, et al. . New England Journal of Medicine (2015) PMID: 25773378